*Result*: Measuring outcomes in adults with spinal muscular atrophy - challenges and future directions - meeting report
*Author/editor-in-chief*:
Sansone, Valeria A. (Verfasser); Walter, Maggie C. (Verfasser) ; Attarian, Sharam (Verfasser); Delstanche, Stéphanie (Verfasser); Mercuri, Eugenio (Verfasser); Lochmüller, Hanns (Verfasser) ; Neuwirth, Christoph (Verfasser) ; Vazquez-Costa, Juan Francisco (Verfasser); Kleinschnitz, Christoph (Verfasser) ; Hagenacker, Tim (Verfasser)
*Publication*:
Freiburg : Universität, 2025
*Physical description scale*:
1 Online-Ressource
*Format*:
*Language*:
*eng*
*Notes*:
Journal of neuromuscular diseases. - 7, 4 (2020) , 523-534, ISSN: 2214-3602
*Subject Added Keywords*:
*DOI*:
10.3233/jnd-200534