*Result*: Long-term efficacy and safety of nusinersen in adults with 5q spinal muscular atrophy: a prospective European multinational observational study

*Publication*:
Freiburg : Universität, 2024
*Physical description scale*:
1 Online-Ressource
*Format*:
*eBook*
*Language*:
*eng*
*Notes*:
The lancet. - 39 (2024) , 100862, ISSN: 2666-7762
*DOI*:
10.1016/j.lanepe.2024.100862