*Result*: T-cell gene therapy for perforin deficiency corrects cytotoxicity defects and prevents hemophagocytic lymphohistiocytosis manifestations
*Author/editor-in-chief*:
Ghosh, Sujal (Verfasser) ; Carmo, Marlene (Verfasser); Calero-Garcia, Miguel (Verfasser); Ricciardelli, Ida (Verfasser); Bustamante Ogando, Juan Carlos (Verfasser); Blundell, Michael P. (Verfasser); Schambach, Axel (Verfasser) ; Ashton-Rickardt, Philip G. (Verfasser); Booth, Claire (Verfasser); Ehl, Stephan (Verfasser) ; Lehmberg, Kai (Verfasser) ; Thrasher, Adrian J. (Verfasser); Gaspar, Hubert Bobby (Verfasser)
*Publication*:
Freiburg : Universität, 2019
*Physical description scale*:
1 Online-Ressource
*Format*:
*Language*:
*eng*
*Notes*:
The journal of allergy and clinical immunology. - 142, 3 (2018) , 904-913.e3, ISSN: 1097-6825
*DOI*:
10.1016/j.jaci.2017.11.050