*Result*: Improved upper limb function in non-ambulant children with SMA type 2 and 3 during nusinersen treatment: a prospective 3-years SMArtCARE registry study
*Author/editor-in-chief*:
Pechmann, Astrid (Verfasser) ; Behrens, Max (Verfasser) ; Dörnbrack, Katharina (Verfasser) ; Tassoni, Adrian (Verfasser) ; Wenzel, Franziska (Verfasser) ; Stein, Sabine (Verfasser) ; Vogt, Sibylle (Verfasser) ; Zöller, Daniela (Verfasser) ; Lochmüller, Hanns (Verfasser) ; Kirschner, Janbernd (Verfasser)
*Publication*:
Freiburg : Universität, 2022
*Physical description scale*:
1 Online-Ressource
*Format*:
*Language*:
*eng*
*Notes*:
Orphanet journal of rare diseases. - 17, 1 (2022) , 384, ISSN: 1750-1172
*DOI*:
10.1186/s13023-022-02547-8