*Result*: Targeted gene correction of human hematopoietic stem cells for the treatment of Wiskott - Aldrich Syndrome
*Author/editor-in-chief*:
Rai, Rajeev (Verfasser); Romito, Marianna (Verfasser) ; Rivers, Elizabeth (Verfasser); Turchiano, Giandomenico (Verfasser) ; Blattner, Georges (Verfasser); Vetharoy, Winston (Verfasser); Ladon, Dariusz (Verfasser); Geoffroy, Andrieux (Verfasser) ; Zhang, Fang (Verfasser); Zinicola, Marta (Verfasser); Leon-Rico, Diego (Verfasser); Santilli, Giorgia (Verfasser); Thrasher, Adrian J. (Verfasser); Cavazza, Alessia (Verfasser)
*Publication*:
Freiburg : Universität, 2020
*Physical description scale*:
Online-Ressource
*Format*:
*Language*:
*eng*
*Notes*:
Nature communications
11, 1 (2020) , 4034, ISSN: 2041-1723
11, 1 (2020) , 4034, ISSN: 2041-1723
*DOI*:
10.1038/s41467-020-17626-2