*Result*: Respiratory function in 192 adult patients with spinal muscular atrophy (SMA) treated with nusinersen – a multicenter observational study

*Publication*:
Freiburg : Universität, 2025
*Physical description scale*:
1 Online-Ressource
*Format*:
*eBook*
*Language*:
*eng*
*Notes*:
Orphanet journal of rare diseases. - 20, 1 (2025) , 476, ISSN: 1750-1172
*DOI*:
10.1186/s13023-025-04009-3