*Result*: Experiences of caregivers of children with spinal muscular atrophy participating in the expanded access program for nusinersen: a longitudinal qualitative study

*Publication*:
Freiburg : Universität, 2020
*Physical description scale*:
Online-Ressource
*Format*:
*eBook*
*Language*:
*eng*
*Notes*:
Orphanet journal of rare diseases
15, 1 (2020) , 194, ISSN: 1750-1172
*Subject Added Keywords*:
*DOI*:
10.1186/s13023-020-01477-7