Result: Nusinersen initiated in infants during the presymptomatic stage of spinal muscular atrophy: Interim efficacy and safety results from the Phase 2 NURTURE study

*Title*:

*Author/editor-in-chief*:

*Publication*:

Freiburg : Universität, 2020

*Physical description scale*:

Online-Ressource

*Format*:

*eBook*

*Language*:

*eng*

*Notes*:

Neuromuscular disorders
29, 11 (2019) , 842-856, ISSN: 1873-2364

*DOI*:

10.1016/j.nmd.2019.09.007

*Result*: Nusinersen initiated in infants during the presymptomatic stage of spinal muscular atrophy: Interim efficacy and safety results from the Phase 2 NURTURE study